FDA Grants Conditional Approval For PTC Therapeutics' Gene Therapy As First Ever With Direct Administration In Brain
PTC Therapeutics' Kebilidi gains FDA accelerated approval as the first brain-administered gene therapy in the U.S. for AADC ...
FiercePharma6h
PTC wins FDA approval for first brain-delivered gene therapy Kebilidi
The FDA issued its first stamp of approval for a cell or gene therapy back in 2017 to Novartis' Kymriah. | The gene therapy ...
The Pharma Letter6h
FDA nod for AADC deficiency gene therapy from PTC
The US Food and Drug Administration (FDA) has granted accelerated approval of PTC Therapeutics’ gene therapy for the ...
Pharmaceutical Technology7h
FDA grants accelerated approval for PTC’s AADC deficiency gene therapy
The US Food and Drug Administration (FDA) has granted accelerated approval for PTC Therapeutics’ KEBILIDI, the first gene ...
Yahoo News12h
Potential Tropical Cyclone 19: Tropical system to become Tropical Storm Sara, Florida impact possible
On Wednesday, PTC 19, formerly known as Invest 99L, was over 400 miles east of Isla Guanaja, Honduras, and 290 miles ...
Finanznachrichten13h
PTC Therapeutics, Inc.: PTC Therapeutics Announces FDA Approval of AADC Deficiency Gene Therapy
"PTC has once again pioneered a new approach to treating highly ... All events were reported within 3 months of administration and 2 events required hospitalization. Monitor patients for signs and ...
ENDPOINTS NEWS16h
FDA ap­proves PTC’s ul­tra-rare dis­ease gene ther­a­py for broad­er pa­tient pop­u­la­tion than Eu­rope
The FDA has cleared PTC Ther­a­peu­tics’ gene ther­a­py for AADC de­fi­cien­cy, an ul­tra-rare dis­ease that im­pacts the ...
katc20h
Potential Tropical Cyclone Nineteen forms in the southwestern Caribbean
Potential Tropical Cyclone Nineteen (PTC 19) has formed in the western Caribbean. This system will likely to develop into the ...
Reuters23h
US FDA approves PTC Therapeutics' gene therapy for ultra-rare disorder
PTC Therapeutics' gene therapy is already approved in the European ... The company said it plans to monetize the voucher.
Hosted on MSN1d
Potential Tropical Cyclone Nineteen forms in the Caribbean
PTC 19 is expected to become Tropical Storm Sara by the end of the week.
Stockhouse1d
PTC Therapeutics Announces FDA Approval of AADC Deficiency Gene Therapy
"PTC has once again pioneered a new approach to treating highly ... All events were reported within 3 months of administration and 2 events required hospitalization. Monitor patients for signs and ...
moneycontrol.com6d
PTC India Financial Services
PTC INDIA FINANCIAL SERVICES LTD.has informed BSE that the meeting of the Board of Directors of the Company is scheduled on 30/07/2024 ,inter alia, to ...